The mission of Canavan Disease Research is to direct funding towards research aimed at developing therapies to treat and cure Canavan disease while networking families to form an educated community poised to reach the clinic. Our efforts have resulted in three gene therapy clinical trials. We have also funded the development of a combination of medicines to slow the progression of Canavan disease and help treat Canavan disease symptoms in some children; this is known as the "Canavan Cocktail." Canavan disease is a neurological disorder. Canavan Disease Research gene therapy trials funded by CRI have helped dozens of children live longer, healthier, and happier lives.

Canavan Disease Research was created by Ilyce Randell to manage and proliferate the larger national and international interests and collaborative efforts of Canavan Research Illinois (CRI). Ilyce Randell is the CoFounder, President, and Director of Patient Advocacy for CRI and CDR. Ilyce also writes and contributes stories for publication to The Mighty. As the parent of an affected child, she uses her experience to help other families affected by Canavan disease. Stories such as "To The Parents Seeking Experimental Medicine For Their Children" can aid families going through similar experiences. Check out our Partner Page on The Mighty. Canavan Disease Research is dedicated to helping children and families affected by Canavan disease, a genetic disorder.

Ilyce Randell, through Canavan Disease Research, has successfully launched the world's first patient registry (the Canavan PIN). The PIN (Patient Insight Network) can help unite Canavan families throughout the world and enable us to gain a better understanding of the true incidence and prevalence of Canavan disease worldwide. This initiative is currently the only international registry for families affected by Canavan disease and the largest database of Canavan patients in the world.